Charlotte Dravet (July 14, 1936 – May 10, 2025)
Dr. Charlotte Dravet (July 14, 1936 – May 10, 2025), the esteemed French pediatric psychiatrist and epileptologist, renowned globally for her pioneering contributions to epilepsy research, passed away, leaving behind a profound legacy in the field of child neurology. Her…
News
Robert Rust
The ICNA along with the global child neurology community mourns the passing of Professor Robert S. Rust, MD. A towering figure in pediatric neurology, Dr. Rust was a true Renaissance man—a historian, physician, educator, mentor, scientist, ethicist, archivist, and humanitarian.…
FDA Approves First-Ever Brain-Injected Gene Therapy for AADC Deficiency
November 19, 2024 The U.S. Food and Drug Administration (FDA) has granted fast-track approval to Kebilidi (Eladocagene exuparvovec), the first gene therapy in the United States administered via direct intracerebral injection. This approval represents a significant advance in the…
Advances in In-Utero Neurological Therapies: A New Era in Prenatal Care
Neurological disorders cause significant morbidity and mortality in children. However, cutting-edge in-utero therapies are transforming the…
First Gene Therapy for Children with Metachromatic Leukodystrophy
Lenmeldy (atidarsagene autotemcel) has received approval from the U.S. Food and Drug Administration. This marks a significant milestone as…
Support the children and their families impacted by the Earthquake in Türkiye & Syria
At least two powerful earthquakes struck in southern Turkey and northern Syria in the early hours of Feb. 6. At least 6,200 people have…
Michael V Johnston [1946 - 2022]
I am deeply saddened to learn that Michael V Johnston MD. Professor Emeritus of Pediatrics and Neurology at the Johns Hopkins University…
